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Why my patient advocacy organization is investing in CRISPR

In last year’s action film “Rampage,” which featured Dwayne “The Rock” Johnson, CRISPR gene-editing technology turns a gorilla, a wolf, and a crocodile into monsters the size of skyscrapers that destroy Chicago.

If you missed the movie, you may have caught wind of He Jiankui. Near the end of 2018, the Chinese scientist reported having used CRISPR to produce the first-ever gene-edited babies. (He currently faces criminal charges in his home country for violating national guidelines, not to mention global scientific ethical standards.)

As the mother of a son with Duchenne muscular dystrophy, a cruel genetic disease that breaks down muscle until the body can no longer function, I don’t see CRISPR as scary or dangerous. To me, it represents the best hope we have for curing my son’s disease and possibly many others. I believe CRISPR is a weapon — not a giant gorilla type of weapon — but a quiet, surgically precise weapon against diseases that have long confounded the scientific community.

Why My Patient Advocacy Organization Is Investing In CRISPR