Single CRISPR Treatment Provides Long-Term Benefits in Mice | DuchenneXchange

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Single CRISPR Treatment Provides Long-Term Benefits in Mice


Researchers at Duke University have shown that a single systemic treatment using CRISPR genome editing technology can safely and stably correct a genetic disease — Duchenne muscular dystrophy (DMD) — for more than a year in mice, despite observed immune responses and alternative gene editing outcomes.

The study appears online on February 18in the journal Nature Medicine.

Single CRISPR Treatment Provides Long-Term Benefits In Mice