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UCLA research could be first step toward healing the hearts of children with Duchenne
After a progressive weakening of the muscles takes away their motor skills, and then their abilities to stand and walk, most males with Duchenne muscular dystrophy die of heart and respiratory failure in their 20s.
Now, researchers at the David Geffen School of Medicine at UCLA are pursuing a cutting-edge way to stop heart disease in patients with Duchenne, which affects one in 5,000 male babies born in the United States. Their work, which is supported by a David Geffen School of Medicine Seed Grant, is just one of a number of projects underway at the medical school in which interdisciplinary groups of UCLA researchers are pursuing new treatments and cures.
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Crispr Halted Muscular Dystrophy In Dogs. Someday, It Might Cure Humans.Today, our partner Dr. Eric Olson and hi...
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New CRISPR Method Takes on Duchenne Muscular DystrophyThe advance of CRISPR gene editing techn...
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Jacques P. Tremblay, PhDDr. Tremblay’s laboratory is renowned ...
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Dr. Eric Olson CRISPR/Cas9 Presentation at CureDuchenne Careshttps://www.youtube.com/watch?v=P-Q8HFXk...
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New lab technology could reveal treatments for muscle-wasting diseaseResearchers from Queen Mary University o...
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UT researcher, with CureDuchenne support, launches company to treat DMD using CRISPR/Cas9 technologyEric Olson, a molecular biologist, has s...