welcome to DuchenneXchange
- a positively charged Duchenne muscular dystrophy community.- join today!
- login
UK patients gain early access to Duchenne drug
UK patients can gain access to Santhera’s as-yet unapproved Duchenne muscular dystrophy drug via an early access scheme.
The Medicines and Healthcare products Regulatory Agency granted Raxone (idebenone) a positive scientific opinion through the Early Access to Medicines Scheme (EAMS).
As a result of the decision, patients aged 10 and above with respiratory function decline, who are not taking gluticorticoids, will be able to get access to Raxone ahead of formal approval by the European Medicines Agency.
rareRelated
-
Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD)The aim of this Phase III study was to a...
-
A Phase III Double-blind Study With Idebenone in Patients With Duchenne Muscular Dystrophy (DMD) Taking Glucocortico...The purpose of the study is to assess th...
-
Santhera PharmaceuticalsSanthera Pharmaceuticals (SIX: SANN) is ...
-
Santhera’s Raxone® receives first positive EAMS scientific opinion from UK’s MHRA in Duchenne muscular ...The aim of the EAMS is to provide patien...
-
Idebenone reduces respiratory complications in patients with Duchenne muscular dystrophyIn Duchenne muscular dystrophy (DMD), pr...
-
CureDuchenne – Treating the Whole DiseaseDuchenne muscular dystrophy is a multifa...
-
Santhera Enters into Agreement to Acquire Option from Idorsia for Exclusive Sub-License of First-in-class Dissociati...Santhera Pharmaceuticals and Idorsia Ltd...