Duchenne Muscular Dystrophy Gallery by a Grandparent

rareRelated

• rareHub
  A safety and efficacy study of ATL1102 in patients with Duchenne muscular dystrophy

  Current DMD therapies are aimed at incre...
• social & media
  My wheels keep rolling

  In this autobiography, I aim to showcase...
• social & media
  Joy in Jackson’s Journey

  Each year I like to go into the local sc...
• evidence & education
  Potential Mechanisms for Prolonged Loss of Ambulation with Deflazacort in Duchenne Muscular Dystrophy – Tolera...

  Objective: To summarize prolonged loss ...
• news & meetings
  Inspired by son, family creates Virginia travel guide for people with disabilities

  Resources/Patient SupportIf he’d h...
• news & meetings
  FDA grants RASRx1902 orphan drug status as potential therapy for Duchenne muscular dystrophy

  The U.S. Food and Drug Administration ha...
• rareHub
  Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular Dystrophy

  The expanded access program will provide...