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A Prospective Natural History Study of Progression of Subjects With Duchenne Muscular Dystrophy

key information

study id #: NCT01753804

condition: Duchenne Muscular Dystrophy

status: terminated


To characterize the natural history and progression of Duchenne Muscular Dystrophy (DMD) to help inform the design of future studies, to capture biomarkers of safety and disease progression and to provide comparative data for the development of rare exons for which formal controlled trials are not feasible.

intervention: Observational study

mechanism of action: No pharmaceutical intervention

results: https://clinicaltrials.gov/ct2/show/results/NCT01753804

last updated: November 22, 2018