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A Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)

key information

study id #: NCT02760264

condition: Duchenne Muscular Dystrophy

status: completed


The purpose of this study is to determine whether a new medication called vamorolone is safe and well-tolerated by boys with Duchenne muscular dystrophy (DMD) ages >= 4 and < 7 years old.

Vamorolone 0.25 mg/kg/day, Vamorolone 0.75 mg/kg/day, Vamorolone 2.0 mg/kg/day, Vamorolone 6.0 mg/kg/day

mechanism of action: Glucocorticoid to delay decline in muscle strength

results: https://clinicaltrials.gov/ct2/show/results/NCT02760264

last updated: January 07, 2019