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enrolling by invitation

An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy

key information

study id #: NCT03532542

condition: Duchenne Muscular Dystrophy

status: enrolling by invitation

purpose:

The main objective of this study is to evaluate the safety and tolerability of long-term treatment with casimersen or golodirsen in patients with Duchenne muscular dystrophy (DMD).

intervention: Casimersen, Golodirsen

mechanism of action: Exon-skipping to promote dystrophin production

results: https://clinicaltrials.gov/ct2/show/results/NCT03532542

last updated: December 04, 2019