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rareClinical
unknown status

Duchenne Muscular Dystrophy Tissue Bank for Exon Skipping

key information

study id #: NCT01772043

condition: Duchenne Muscular Dystrophy

status: unknown

purpose:

We will utilize the Cooperative International Neuromuscular Research Group (CINRG) network to collect and store tissue and blood from patients with Duchenne muscular dystrophy (DMD) with specific genetic mutations within the dystrophin gene that could be treated by antisense oligonucleotide (AO) drugs.

mechanism of action: No pharmaceutical intervention

results: https://clinicaltrials.gov/ct2/show/results/NCT01772043

last updated: November 22, 2018

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