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Exploratory Study of NS-065/NCNP-01 in DMD

key information

study id #: NCT02081625

condition: Duchenne Muscular Dystrophy

status: completed


This study is designed to assess the safety, tolerability, efficacy and pharmacokinetics (PK) of NS-065/NCNP-01 in subjects diagnosed with Duchenne muscular dystrophy (DMD).

intervention: NS-065/NCNP-01

mechanism of action: Exon-skipping to promote dystrophin production

results: https://clinicaltrials.gov/ct2/show/results/NCT02081625

last updated: March 11, 2020