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Extension Study of BMN 044 in Duchenne Muscular Dystrophy (DMD)

key information

study id #: NCT02958202

condition: Duchenne Muscular Dystrophy

status: terminated


The aim of this study is to provide continuing access to BMN 044 treatment for subjects previously treated with BMN 044. The information gained from this study is expected to further characterize the efficacy and safety of BMN 044 over a longer treatment period.

intervention: BMN 044 IV 6 mg/kg, BMN 044 IV 9 mg/kg, BMN 044 SC 6 mg/kg

mechanism of action: Exon-skipping to promote dystrophin production

results: https://clinicaltrials.gov/ct2/show/results/NCT02958202

last updated: November 22, 2018