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active, not recruiting

Extension Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD)

key information

study id #: NCT03167255

condition: Duchenne Muscular Dystrophy

status: active, not recruiting


This is an open-label, extension study of NS-065/NCNP-01 administered intravenously once weekly for an additional 168 weeks to boys with DMD who complete Study NS-065/NCNP-01-201.

intervention: NS-065/NCNP-01

mechanism of action: Exon-skipping to promote dystrophin production

results: https://clinicaltrials.gov/ct2/show/results/NCT03167255

last updated: May 03, 2020