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A Gene Delivery Study to Evaluate the Safety of and Expression From SRP-9001 in Duchenne Muscular Dystrophy (DMD)

key information

study id #: NCT04626674

condition: Muscular Dystrophy, Duchenne

status: not yet recruiting


This is an open-label gene delivery study evaluating the safety of and expression from SRP-9001 in individuals with Duchenne Muscular Dystrophy over 260 weeks.

intervention: SRP-9001

mechanism of action: Gene therapy to introduce a version of dystrophin

results: https://clinicaltrials.gov/ct2/show/results/NCT04626674

last updated: November 18, 2020