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enrolling by invitation

Long-term, Extension Study of DS-5141b in Patients With Duchenne Muscular Dystrophy

key information

study id #: NCT04433234

condition: Duchenne Muscular Dystrophy

status: Enrolling by invitation


This is a multicenter, open-label, long-term, extension, phase 2 study to evaluate the safety and efficacy of long-term treatment with DS-5141b in patients with DMD who have completed DS5141-A-J101.

intervention: DS-5141b

mechanism of action: Exon-skipping to promote dystrophin production

results: https://clinicaltrials.gov/ct2/show/results/NCT04433234

last updated: August 14, 2020