welcome to DuchenneXchange
- a positively charged Duchenne muscular dystrophy community.- join today!
- log in
Long-term, Extension Study of DS-5141b in Patients With Duchenne Muscular Dystrophy
study id #: NCT04433234
condition: Duchenne Muscular Dystrophy
status: Enrolling by invitation
purpose:This is a multicenter, open-label, long-term, extension, phase 2 study to evaluate the safety and efficacy of long-term treatment with DS-5141b in patients with DMD who have completed DS5141-A-J101.
intervention: DS-5141b
mechanism of action: Exon-skipping to promote dystrophin production
results: https://clinicaltrials.gov/ct2/show/results/NCT04433234
last updated: August 14, 2020
rareRelated
-
Study of DS-5141b in Patients With Duchenne Muscular DystrophyThis is a phase I/II study to evaluate t...
-
Insurers battle families over costly drug for fatal diseaseNolan and Jack Willis, twins from upstat...
-
Safety and Dose Finding Study of NS-065/NCNP-01 in Boys With Duchenne Muscular Dystrophy (DMD)The main objective of this study is to e...
-
Exon Skipping and Stop Codon Read-ThroughThe DMD gene is made up of 79 pieces cal...
-
Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular DystrophyThis is an open-label study to assess th...
-
Sarepta Therapeutics Statement on ICER Draft Evidence Report for Treatments for Duchenne Muscular DystrophySarepta Therapeutics, Inc., the leader...
-
Open Label, Extension Study of PRO044 in Duchenne Muscular Dystrophy (DMD)The purpose of this study is to see whet...
-
Eteplirsen, a Phosphorodiamidate Morpholino Oligomer (PMO) for Duchenne Muscular Dystrophy (DMD): Clinical Update an...Objective: DMD, a rare, degenerative, X...
-
Duchenne Muscular Dystrophy: New Analysis Shows Drug Slows Down Respiratory DeclineDuchenne muscular dystrophy occurs in bo...