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Modified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced Diet

key information

study id #: NCT02383511

condition: Duchenne Muscular Dystrophy

status: completed


Placebo-controlled, multi-centre, randomized, double-blind dose escalation study. The aim is to evaluate the pharmacokinetics (PK) and safety of SMT C1100 in paediatric patients with Duchenne Muscular Dystrophy (DMD) who follow a balanced diet.

intervention: SMT C1100

mechanism of action: Utophin modulator to promote utophin production

results: https://clinicaltrials.gov/ct2/show/results/NCT02383511

last updated: November 22, 2018