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enrolling by invitation

Exploratory Study of NS-089/NCNP-02 in DMD

key information

study id #: NCT04129294

condition: Duchenne Muscular Dystrophy

status: enrolling by invitation

purpose:

This study is designed to assess the safety, tolerability, efficacy and pharmacokinetics (PK) of NS-089/NCNP-02 in subjects diagnosed with Duchenne muscular dystrophy (DMD), and to determine the dosage for subsequent studies.

intervention: NS-089/NCNP-02

mechanism of action: Exon-skipping to promote dystrophin production

results: https://clinicaltrials.gov/ct2/show/results/NCT04129294

last updated: December 10, 2019