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Open Label Extension Study of HT-100 in Patients With DMD
study id #: NCT01978366
condition: Duchenne Muscular Dystrophy
status: terminated
purpose:This study is designed to provide 6-months continuous dosing with the study medication, called HT-100, on participants who successfully completed the predecessor study (HALO-DMD-01). The main purpose of this study is to assess chronic safety, tolerability, pharmacodynamic activity (testing the drug’s effect on DMD) and population pharmacokinetics (measuring how much drug is in the bloodstream) in participants with a broad spectrum of Duchenne muscular dystrophy (DMD).
intervention: HT-100
mechanism of action: Small molecule designed to reduce fibrosis and inflammation
results: https://clinicaltrials.gov/ct2/show/results/NCT01978366
last updated: September 08, 2020
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