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Scientific Articles

Duchenne Muscular Dystrophy Awaits Gene Therapy

key information

source: Nature Biotechnology

year: 2019

authors: Jones D

summary/abstract:

Solid’s gene therapy disappoints in the clinic, but other gene therapies and exon-skipping agents continue their march, with CRISPR on the way.

organization: Brighton, UK

DOI: 10.1038/s41587-019-0103-5

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