source: Muscular Dystrophy UK
A chemical substance which helps to transmit a signal from the nerve to the muscle causing it to contract.
Acetylcholine receptors (AChRs)
Proteins found in the membrane surrounding the muscle cell to which acetylcholine binds.
Adeno-associated virus (AAV)
AAV (Adeno-Associated Virus) is a small virus, which infects humans and some other primate species. AAV is not currently known to cause disease and causes a very mild immune response. These features make AAV a very attractive vehicle for delivering genes into cells (gene therapy).
The ‘building blocks’ of proteins. The sequence of amino acids determines the shape, properties and role of the protein.