Understanding Neuromuscular Disease Care | DuchenneXchange

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Understanding Neuromuscular Disease Care

key information

source: IQVIA Institute Report

year: 2018

summary/abstract:

Neuromuscular diseases (NMD) encompass a broad group of disorders that collectively impact an estimated 250,000 patients in United States. Currently, treatment options for these diseases are limited; however, the financial impact is staggering with costs related to neuromuscular disease exceeding $46 billion dollars annually. This new report, funded by the Muscular Dystrophy Association (MDA), shows that advancements in genetic testing and precision medicine will radically alter the course of neuromuscular disease within the next decade. The report illuminates the role that big data technologies will play in revolutionizing the importance of new-born early genetic screening, intervention and treatment as a pathway to accelerating new therapies. The MDA, with the advent of their comprehensive data hub, MOVR, is driving the advancement of research, new technologies and care strategies to galvanize both the industry and research arenas to pioneer better care and more cures.

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