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Michael Young, 9, wrote a letter to Scottish First Minister Nicola Sturgeon, urging her to help make the drug Translarna available for people with muscular dystrophy. Young has Duchenne muscular dystrophy, a genetic disorder characterized by progressive muscle degeneration and weakness. He relies on Translarna, and his family is campaigning for the NHS to support the use of the drug, currently available in other countries in Europe.
My name is Michael Young (age 9) and I have Duchenne muscular dystrophy. I NEED your help. I have medicine called Translarna. Some boys have the same problem as me but don’t get the medicine. We need (you and me) to help Duchenne boys, because it is not something that a lot of people know about and the boys need medicine. If my medicine is stopped I will need a wheelchair. Please can I meet with you so that you can help boys to keep walking and get Translarna. I can meet you anytime and anywhere.
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