welcome to DuchenneXchange

- a positively charged Duchenne muscular dystrophy community.
  • join today!

Nearly Half of Duchenne Muscular Dystrophy Patients Are Candidates for Gene Therapies


More than 40 percent of boys with Duchenne muscular dystrophy (DMD) in a large genetic testing database are candidates for either approved genetically targeted therapies or treatments in clinical development, according to a study presented here at the annual meeting of the American Association of Neuromuscular & Electrodiagnostic Medicine.